Data for Roche’s Evrysdi® (risdiplam) published in New England Journal of Medicine shows significant improvement in survival and motor milestones in babies with Type 1 spinal muscular atrophy (SMA)
FIREFISH Part 2 study showed treatment with Evrysdi helped babies stay free of permanent ventilation, sit without support and improve across a range of motor milestones Evrysdi has proven efficacy in adults, children and babies two months and older with over 4,000 patients treated to date SMA is the leading genetic cause of death in... Read more